Duchenne Muscular Dystrophy Insights

This week's must-know community updates, latest research & events

March 26, 2025

New Report: Introduction to Cell Therapy

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Latest Research

In a recent study, researchers explored using machine learning-based radiomics with MRI to differentiate between early-stage Duchenne muscular dystrophy (DMD) and Becker muscular dystrophy (BMD) in children. This is important because both conditions present similar symptoms early on, making diagnosis challenging. The study by Chen et al. (2025) aims to improve diagnostic accuracy using advanced imaging techniques.

The ability to distinguish between DMD and BMD early on could significantly impact treatment and management strategies. While the study's details are not fully disclosed, it highlights the potential for advanced imaging and machine learning to enhance diagnostic precision in muscular dystrophies. This could lead to more personalized care plans for patients with these conditions. Further research in this area may help improve outcomes for those affected by these diseases.

Clinical Trials

This is a list of upcoming or ongoing clinical trials that are actively recruiting and have been listed or updated in the last two weeks:

Evaluation of the Safety and Efficacy of BBM-D101 to Treat Patients with Duchenne Muscular Dystrophy

Trial of Cell Based Therapy for DMD

A Gene Delivery Study to Evaluate the Safety and Expression of Delandistrogene Moxeparvovec in Participants Under the Age of Four With Duchenne Muscular Dystrophy (DMD)

Gamified Occupational Therapy for Adolescents with Duchenne Muscular Dystrophy

View the full list of clinical trials →

Community News

Parent Project Muscular DystrophyMar 19, 2025

We are humbled and grateful to share that #Duchenne muscular dystrophy has been recommended by House and Senate Defense Appropriations leadership for $12.5 million in federal funding for Fiscal Year 2025 through the Congressionally Directed Medical Research Programs at the Department of Defense.

This achievement reflects the tireless efforts of our community—the families who have shared their stories, the researchers dedicated to improving the lives of those living with Duchenne, and the advocates who have relentlessly pushed for increased funding. To every advocate who has raised their voice, thank you. Our work is far from over, but today, we take a moment to acknowledge the power of advocacy and the collective impact we can make.

Muscular Dystrophy UKMar 18, 2025

Over half of people with muscle wasting and weakening conditions receive Personal Independence Payments (PIP). It's a lifeline. We’re very disappointed the UK Government will proceed with cuts that leave us more financially insecure, affect our health and quality of life. It will damage our ability to work, not improve it.

Many people living with muscle wasting and weakening conditions do work. With the right support, more could work. But these short-term cuts and pressure to put more people into work who currently don't or can't, will have lasting consequences.

We know the welfare system needs a significant overhaul. But wanting to cut costs is the wrong way to go. Many people today will be very concerned the UK Government has decided to cut PIP and alarmed and worried about the changes.

In the next few days, we’ll be looking at the details of the consultation to better understand how these will impact people with muscle wasting and weakening conditions. We’ll share more details as well as how you can get involved.

We will also:

Work with other disability organisations to oppose cuts to these vital benefits and make the case for reform.

Respond to today’s consultation to share the concerns and needs of people with muscle wasting and weakening conditions.

If you have any concerns, we’re here for you. Call our helpline 0800 652 6352 or email [email protected]

Muscular Dystrophy CanadaMar 21, 2025

Champions don’t stop when they reach the finish line. They keep going, pushing limits, and breaking barriers. Today, we’re proud to announce that Paralympic champion, award-winning speaker, author, coach, and fierce advocate Danielle Campo is stepping up as Muscular Dystrophy Canada’s new National Ambassador.

From breaking world records to breaking barriers for the neuromuscular community, her journey continues. Welcome home, Danielle.

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