Duchenne Muscular Dystrophy Insights

My Son Has Duchenne Muscular Dystrophy; Screening Babies Would Help

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Latest Research

A recent study highlights the high prevalence of metabolic syndrome and insulin resistance among Thai children with Duchenne Muscular Dystrophy (DMD).

Thamcharoenvipas et al.

(2025)
This condition, characterized by progressive muscle weakness, is linked to increased cardiovascular risks partly due to obesity and cardiomyopathy, a disease affecting the heart muscle.

These findings emphasize the importance of early screening for metabolic issues to better manage the health of children with DMD Thamcharoenvipas et al.

(2025)
.

The study underscores the need to monitor and manage metabolic syndrome and insulin resistance, conditions that increase the risk of heart disease, stroke, and type 2 diabetes.

Insulin resistance occurs when the body's cells do not respond effectively to insulin, causing high blood sugar levels.

Early detection and treatment of these metabolic conditions could help reduce some long-term health complications associated with DMD.

Clinical Trials

This is a list of upcoming or ongoing clinical trials that are actively recruiting and have been listed or updated in the last two weeks:
A Gene Delivery Study to Evaluate the Safety and Expression of Delandistrogene Moxeparvovec in Participants Under the Age of Four With Duchenne Muscular Dystrophy (DMD)
Study Type
Phase II
Location
6 countries
Age Range
0 - 3 Years
Enrollment
21
A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
Study Type
Phase II
Location
2 countries
Age Range
4 - 11 Years
Enrollment
43
A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Non-Ambulatory and Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)
Study Type
Phase III
Location
13 countries
Age Range
0 - Not specified
Enrollment
148
DMD Voice: Qualitative Interviews With Patients and Caregivers
Study Type
Observational
Location
Pennsylvania
Age Range
10+ Years
Enrollment
68

Community News

Muscular Dystrophy UKMuscular Dystrophy UKApr 17, 2025

Giveaway time!

We’re giving you the chance to WIN this amazing bundle including the newly published book 'Who Wants Normal' by Frances Ryan – for FREE! 💥

What’s up for grabs:

🧡 A branded t-shirt

👜 Branded tote bag

📚 Who Wants Normal? by Frances Ryan

📝 Notebook and a pen

To enter:

1️⃣ Like this post

2️⃣ Follow us

3️⃣ Tag a friend who’d love to win too!

Bonus entry if you share this post!

Closes: Thursday 24 April 2025

Muscular Dystrophy CanadaMuscular Dystrophy CanadaApr 16, 2025

This weekend, Fire Fighters are hosting boot drives to raise critical funds and awareness for Muscular Dystrophy Canada. Come, #FillTheBoot in your area, and help our Fire Fighter partners break down barriers for Canadians affected by #NeuromuscularDisorders.

Every dollar raised helps us fund critical research, deliver programs and services and influence positive public policy changes.

To learn more about how you make a difference, visit www.filltheboot.ca.

Muscular Dystrophy Canada Post
Muscular Dystrophy AssociationMuscular Dystrophy AssociationApr 17, 2025

Rhys Hoskins, MLB player for the Milwaukee Brewers and alumni MDA Summer Camp volunteer and longtime supporter shares why volunteering is an experience like no other. MDA Summer Camp is a week-long experience that changes lives—campers and volunteers alike! From building lifelong friendships to making an impact, this week is truly unforgettable. 💙💛

Ready to be a part of something incredible? Sign up to volunteer today! MDA.org/SummerCamp

Muscular Dystrophy Association Post

Upcoming Events

APR
22
Grant Recipients Announcement Online Muscular Dystrophy Canada
APR
23
Cardiac Care Neuromuscular Webinar Online Muscular Dystrophy Association
MAY
06
Accessible Inclusive Sport Discussion Online Muscular Dystrophy NSW