Exciting breakthroughs in rare disease treatments mean more patients are gaining access to cutting-edge therapies - and specialty pharmacies are playing a crucial role in delivering these medications with expert support. But what exactly do they do, and when do they come into play?
AllMyHealth’s latest guide breaks it all down - exploring how specialty pharmacies work, their expanding role in patient care, and how individuals can engage with them. Plus, we spotlight specialty pharmacies such as Orsini and Accredo which provide DMD treatment.
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In their review, Zhao et al. (2025) discuss how the fruit fly, Drosophila melanogaster, is an effective model for studying muscular dystrophy. They highlight the benefits of using this organism, such as its genetic similarity to humans and the ease of manipulating its genes. This has allowed researchers to better understand the disease's progression, the function of specific genes related to muscle health, and to identify potential new targets for treatment.
The review emphasizes the insights gained from Drosophila models, which have been instrumental in unraveling the complex molecular mechanisms of various types of muscular dystrophy. By studying these flies, scientists have been able to explore the genetic underpinnings of muscle weakness and degeneration, which is crucial for developing future therapies.